May 9 – 10, 2024 Meeting

Agenda (PDF - 164 KB)

Meeting Minutes - Pending

Webcast

• May 9, 2024 - Pending
• May 10, 2024 - Pending

Transcripts

• May 9, 2024 - Pending
• May 10, 2024 - Pending

Presentations

Day 1

Regulatory Process for the Review of Drugs for Rare Diseases (PDF - 1 MB)

Anita Zaidi, MD, Lead Physician
Center for Drug Evaluation and Research (CDER) –
U.S. Food and Drug Administration

Duchenne Muscular Dystrophy Evidence-Based Review: Update (PDF - 451 KB)

Alex R. Kemper, M.D., M.P.H., M.S.
Lead Evidence-Based Review Group

ACHDNC Decision Matrix Tool: Public Health System Assessment (PDF - 179 KB)

Ned Calonge, M.D., M.P.H.
Committee Chair

Day 2

ACHDNC Nomination and Evidence Review Process (PDF - 169 KB)

Ned Calonge, M.D., M.P.H.
Committee Chair

Qualitative Evidence Synthesis: GRADE-CERQual Approach For Assessing the Confidence in Synthesized Findings (PDF - 2 MB)

Jane Noyes, M.D., PhD
Professor in Health and Social Services Research and Child Health
Bangor University

Newborn Screening Ad Hoc Topic Groups: Updates and Committee Discussion (PDF - 1 MB)

Jelili Ojodu, M.P.H.
Association of Public Health Laboratories